Paroxysmal Nocturnal Hemoglobinuria - 28 Studies Found Completed : Paroxysmal Nocturnal Hemoglobinuria Human Anti-Human Antibodies Study : Paroxysmal Nocturnal Hemoglobinuria PNH : 2011-08-05 Completed : Transfer of GPI-Linked Proteins to Transfused Patients With Paroxysmal Nocturnal Hemoglobinuria : Paroxysmal Hemoglobinuria : 2002-06-14 Active, not recruiting : A Open-label, Multiple Ascending Dose Study to Evaluate the Efficacy, Safety, Tolerability, Immunogenicity, Pharmacokinetics, and Pharmacodynamics of ALXN1210 Administered Intravenously to Patients With Paroxysmal Nocturnal Hemoglobinuria : Paroxysmal Nocturnal Hemoglobinuria PNH : 2015-11-11 : Biological: Study Drug- ALXN1210 Active, not recruiting : Study of Global Coagulation Tests in Patients With Paroxysmal Nocturnal Haemoglobinuria : Paroxysmal Nocturnal Haemoglobinuria : 2009-11-20 Recruiting : Study to Assess Safety, Efficacy, Pharmacokinetics, and Pharmacodynamics of RO7112689 in Healthy Volunteers and Participants With Paroxysmal Nocturnal Hemoglobinuria : Paroxysmal Hemoglobinuria, Nocturnal : 2016-11-01 : Drug: RO7112689 RO7112689 will Completed : Microvascular and Cardiac Dysfunction in Paroxysmal Nocturnal Hemoglobinuria and Sickle Cell Disease : Rheologic Disease Sickle Cell Disease Paroxysmal Nocturnal Hemoglobinuria : 2015-10-27 : Drug: APL-2 Recruiting : Phase 2 Safety and Efficacy Study of RA101495 to Treat PNH Patients : Paroxysmal Nocturnal Hemoglobinuria (PNH) : 2017-03-08 : Drug: RA101495 0.3mg/kg subcutaneously (SC) at Day 1 (loading dose) followed by a starting maintenance d Active, not recruiting : A Phase I Study to Assess the Safety APL-2 as an Add-On to Standard of Care in Subjects With PNH : Paroxysmal Nocturnal Hemoglobinuria (PNH) : 2014-10-08 : Drug: APL-2 Active, not recruiting : A Phase 1/2 Study of an Investigational Drug, ALN-CC5, in Healthy Adult Volunteers and Patients With PNH : Paroxysmal Nocturnal Hemoglobinuria (PNH) : 2015-01-23 : Drug: ALN-CC5 Single or multip <<< Previous | Next >>>